Why Novel Cancer Vaccine Tested at UCSF Marks New Treatment Era
By Laura López González and Jess Berthold on
PNOC Foundation Launches $50 Million "Lose No Child" Campaign to Transform the Future of Treatment for Kids with Brain Cancer
By PNOC Foundation on
Chan Zuckerberg Initiative, Innovative Genomics Institute Announce New Center for Pediatric CRISPR Cures
By Stacey Bailey on
Going Public: Doudna’s Dream Team Launches Groundbreaking Sickle Cell Trial
By Kevin Davies, PhD on
A publicly funded consortium of University of California (UC) researchers and clinicians is one big step closer to realizing a decade-long plan to launch a CRISPR-based gene-editing trial for sickle cell disease (SCD). Last week, the team, led by 2020 Nobel laureate Jennifer Doudna, PhD, announced…Novel Gene Therapy Trial for Sickle Cell Disease Launches
By Melinda Krigel on
The study uses CRISPR to correct sickle cell mutation and aims to free patients of the disease.
Neurona Therapeutics Receives FDA’s Regenerative Medicine Advanced Therapy (RMAT) Designation for NRTX-1001 in Focal Epilepsy
UCSF Treats First Patient with Homegrown Chimeric Antigen Receptor (CAR) T-cell Therapy
By Cammie Edwards on
This month marked an important milestone for UCSF faculty and clinicians working to take on the challenge of glioblastoma multiforme (GBM). They treated their first patient with a promising chimeric antigen receptor (CAR) T-cell therapy that was fully conceived, designed, optimized and manufactured…
Gene Therapy Is Halting Cancer. Can It Work Against Brain Tumors?
By Suzane Leigh on
Grant of up to $11 million will fund a clinical trial at UCSF that uses a smarter new CAR-T guided by precision technology.
Fetal therapy offers hope for unborn patients suffering from the rare genetic disease Hunter Syndrome
By Molly McCrea and Juliette Goodrich, CBS News Bay Area on
Some parents-to-be have to face the terrifying news that their unborn child has been diagnosed with a life-threatening genetic disorder. But thanks to a medical team at a Bay Area hospital, there is amazing new hope in a fetal therapy that may spare their unborn child serious outcomes. 
New CRISPR Center Brings Hope for Rare and Deadly Genetic Diseases
By Jess Berthold on
CRISPR collaboration combines expertise from three UC schools to scale treatment for diseases that industry has largely passed by – until now.